Long-term outcome and lineage-specific chimerism in 194 patients with Wiskott-Aldrich syndrome treated by hematopoietic cell transplantation in the period 1980-2009: an international collaborative study

Moratto, Daniele; Giliani, Silvia; Bonfim, Carmem; Mazzolari, Evelina; Fischer, Alain; D. Ochs, Hans; J. Cant, Andrew; J. Thrasher, Adrian; J. Cowan, Morton; H. Albert, Michael; N. Small, Trudy; Pai, Sung‐Yun; Haddad, Élie; Lisa, Antonella; Hambleton, Sophie; Slatter, Mary; Cavazzana, Marina; Mahlaoui, Nizar; Pïcard, Capucine; R. Torgerson, Troy; M. Burroughs, Lauri; Koliski, Adriana; Zanis Neto, José; Porta, Fulvio; Qasim, Waseem; Veys, Paul; Kavanau, Kristina; Hönig, Manfred; Schulz, Ansgar; Friedrich, Wilhelm; D. Notarangelo, Luigi

doi:10.1182/blood-2010-11-319376

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Long-term outcome and lineage-specific chimerism in 194 patients with Wiskott-Aldrich syndrome treated by hematopoietic cell transplantation in the period 1980-2009: an international collaborative study

Published in Blood • Jun 10, 2011

Authors:

Daniele Moratto

Silvia Giliani

Carmem Bonfim

Abstract

In this retrospective collaborative study, we have analyzed long-term outcome and donor cell engraftment in 194 patients with Wiskott-Aldrich syndrome (WAS) who have been treated by hematopoietic cell transplantation (HCT) in the period 1980- 2009. Overall survival was 84.0% and was even higher (89....

Subject

Wiskott–Aldrich syndrome

Transplantation

Medicine

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