Nusinersen Dosing Patterns in Patients With Spinal Muscular Atrophy Type 1 in the United States: Findings From a Retrospective Claims Database Analysis (2335)
Published in Neurology • Apr 13, 2021
Authors:
Marjolaine Gauthier‐Loiselle
,
Martin Cloutier
,
Walter Toro Jimenez
Abstract
To investigate dosing patterns in patients with spinal muscular atrophy (SMA) type 1 treated with nusinersen in the United States.
Nusinersen Dosing Patterns in Patients With Spinal Muscular Atrophy Type 1 in the United States: Findings From a Retrospective Claims Database Analysis (2335) | NobleBlocks